FDA approves Vertex/CRISPR Gene Therapy for Inherited Blood Disorders
FDA approves Vertex/CRISPR Gene Therapy for Inherited Blood Disorders In a monumental leap for gene therapy and a beacon of hope for millions suffering from life-threatening blood disorders, the US Food and Drug Administration (FDA) has granted approval to Vertex Pharmaceuticals and CRISPR Therapeutics’ revolutionary treatment – Exa-cel (casgenevo). This breakthrough represents a new era … Read more